Additional data from 4 year update of ongoing phase 1/II study of valoctocogene roxaparvovec gene therapy for severe hemophilia A presented at World Federation of Hemophilia virtual summit.- BioMarin
BioMarin Pharmaceutical Inc. announced additional data from its previously reported four-year update of an open-label Phase 1/II study of valoctocogene roxaparvovec , an investigational gene therapy treatment for… read more.

